HSCT FOR PEDIATRIC DISEASES

Evaluation of Frameworks for HSCT Design Optimization

Pediatric and inherited neurovascular diseases.

Pediatric and inherited neurovascular syndromes have diverse presentations and treatments. Although many of these diseases are uncommon, they must be included in the differential diagnosis for children with strokes or hemorrhages. In neurosurgical practice, familial cavernous malformations, hereditary hemorrhagic telangiectasia (HHT), and moyamoya are the most frequently encountered of these di...

Prospective Surveillance for IFI in HSCT Recipients

Dimitrios P. Kontoyiannis, Kieren A. Marr, Benjamin J. Park, Barbara D. Alexander, Elias J. Anaissie, Thomas J. Walsh, James Ito, David R. Andes, John W. Baddley, Janice M. Brown, Lisa M. Brumble, Alison G. Freifeld, Susan Hadley, Loreen A. Herwaldt, Carol A. Kauffman, Katherine Knapp, G. Marshall Lyon, Vicki A. Morrison, Genovefa Papanicolaou, Thomas F. Patterson, Trish M. Perl, Mindy G. Schus...

Pediatric chronic diseases--stealing childhood.

IT IS EASY TO ROMANTICIZE CHILDHOOD, ESPECIALLY IN THE middle of summer. Memories of lazy days at the beach, playing baseball or double Dutch with friends, catching lightning bugs in a jar and hopefully remembering to let them go, and having no concerns about bills to pay or time pressures or health problems. Perhaps childhood still is that way for some children, but for those with a chronic il...

Emergence of pediatric rare diseases

In this article we discuss the steps taken by the United States (US) and the European Union (EU) to meet the health care needs of children with rare diseases and suggest possible directions for future endeavors for further improvement. We reviewed 23 reports and nine legislative documents related to pediatric rare diseases and public policy. We assessed the outcome measures of access and satisf...